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JCI Insight
Curative in vivo hematopoietic stem cell gene therapy of murine thalassemia using large regulatory elements
- H. Wang
- A. Georgakopoulou
- C. Li
- Z. Liu
- S. Gil
- A. Bashyam
- E. Yannaki
- A. Anagnostopoulos
- A. Pande
- Z. Izsvák
- T. Papayannopoulou
- A. Lieber