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Juni 2018 / Mol Ther Nucleic Acids The antibiotic-free pFAR4 vector paired with the Sleeping Beauty transposon system mediates efficient transgene delivery in human cells M. Pastor S. Johnen N. Harmening M. Quiviger J. Pailloux M. Kropp P. Walter Z. Ivics Z. Izsvák G. Thumann D. Scherman C. Marie 08. Juni 2018 / J Mol Biol Self-assembly of mutant huntingtin exon-1 fragments into large complex fibrillar structures involves nucleated branching A.S. Wagner A.Z. Politi A. Ast K. Bravo-Rodriguez K. Baum A. Buntru N.U. Strempel L. Brusendorf C. Hänig A. Boeddrich S. Plassmann K. Klockmeier J.M. Ramirez-Anguita E. Sanchez-Garcia J. Wolf E.E. Wanker 01. Juni 2018 / J Invest Dermatol SMARCAD1 haploinsufficiency underlies Huriez syndrome and associated skin cancer susceptibility C. Günther M.A. Lee-Kirsch J. Eckhard A. Matanovic T. Kerscher F. Rüschendorf B. Klein N. Berndt N. Zimmermann C. Flachmeier T. Thuß N. Lucas I. Marenholz J. Esparza-Gordillo N. Hübner H. Traupe E. Delaporte Y.A. Lee 15. Juni 2018 / Mol Ther Methods Clin Dev Integrating HDAd5/35++ vectors as a new platform for HSC gene therapy of hemoglobinopathies C. Li N. Psatha H. Wang M. Singh H.B. Samal W. Zhang A. Ehrhardt Z. Izsvák T. Papayannopoulou A. Lieber 01. Juni 2018 / Mol Ther Nucleic Acids The antibiotic-free pFAR4 vector paired with the sleeping beauty transposon sSystem mediates efficient transgene delivery in human cells M. Pastor S. Johnen N. Harmening M. Quiviger J. Pailloux M. Kropp P. Walter Z. Ivics Z. Izsvák G. Thumann D. Scherman C. Marie 01. November 2018 / Eur J Med Genet Improved molecular platform for the gene therapy of rare diseases by liver protein secretion M. Quiviger A. Giannakopoulos S. Verhenne C. Marie E.F. Stavrou K. Vanhoorelbeke Z. Izsvák S.F. De Meyer A. Athanassiadou D. Scherman 30. April 2018 / Genes Nutr ONS: an ontology for a standardized description of interventions and observational studies in nutrition F. Vitali R. Lombardo D. Rivero F. Mattivi P. Franceschi A. Bordoni A. Trimigno F. Capozzi G. Felici F. Taglino F. Miglietta N. De Cock C. Lachat B. De Baets G. De Tré M. Pinart K. Nimptsch T. Pischon J. Bouwman D. Cavalieri 28. Juni 2018 / Cell Physiol Biochem Pathway analysis hints towards beneficial effects of long-term vibration on human chondrocytes R. Lützenberg K. Solano C. Buken J. Sahana S. Riwaldt S. Kopp M. Krüger H. Schulz K. Saar N. Huebner R. Hemmersbach J. Bauer M. Infanger D. Grimm M. Wehland 17. Januar 2018 / Sci Rep The role of NFκB in spheroid formation of human breast cancer cells cultured on the Random Positioning Machine S. Kopp J. Sahana T. Islam A.G. Petersen J. Bauer T.J. Corydon H. Schulz K. Saar N. Huebner L. Slumstrup S. Riwaldt M. Wehland M. Infanger R. Luetzenberg D. Grimm 01. Juli 2018 / Genome Editing in Stem Cells and Regenerative Biology Genome engineering using Sleeping Beauty transposition in vertebrates S.S. Chilkunda V. Raghunathan S.A. Narayanavari Z. Ivics Z. 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01. Juni 2018 / Mol Ther Nucleic Acids The antibiotic-free pFAR4 vector paired with the Sleeping Beauty transposon system mediates efficient transgene delivery in human cells M. Pastor S. Johnen N. Harmening M. Quiviger J. Pailloux M. Kropp P. Walter Z. Ivics Z. Izsvák G. Thumann D. Scherman C. Marie
08. Juni 2018 / J Mol Biol Self-assembly of mutant huntingtin exon-1 fragments into large complex fibrillar structures involves nucleated branching A.S. Wagner A.Z. Politi A. Ast K. Bravo-Rodriguez K. Baum A. Buntru N.U. Strempel L. Brusendorf C. Hänig A. Boeddrich S. Plassmann K. Klockmeier J.M. Ramirez-Anguita E. Sanchez-Garcia J. Wolf E.E. Wanker
01. Juni 2018 / J Invest Dermatol SMARCAD1 haploinsufficiency underlies Huriez syndrome and associated skin cancer susceptibility C. Günther M.A. Lee-Kirsch J. Eckhard A. Matanovic T. Kerscher F. Rüschendorf B. Klein N. Berndt N. Zimmermann C. Flachmeier T. Thuß N. Lucas I. Marenholz J. Esparza-Gordillo N. Hübner H. Traupe E. Delaporte Y.A. Lee
15. Juni 2018 / Mol Ther Methods Clin Dev Integrating HDAd5/35++ vectors as a new platform for HSC gene therapy of hemoglobinopathies C. Li N. Psatha H. Wang M. Singh H.B. Samal W. Zhang A. Ehrhardt Z. Izsvák T. Papayannopoulou A. Lieber
01. Juni 2018 / Mol Ther Nucleic Acids The antibiotic-free pFAR4 vector paired with the sleeping beauty transposon sSystem mediates efficient transgene delivery in human cells M. Pastor S. Johnen N. Harmening M. Quiviger J. Pailloux M. Kropp P. Walter Z. Ivics Z. Izsvák G. Thumann D. Scherman C. Marie
01. November 2018 / Eur J Med Genet Improved molecular platform for the gene therapy of rare diseases by liver protein secretion M. Quiviger A. Giannakopoulos S. Verhenne C. Marie E.F. Stavrou K. Vanhoorelbeke Z. Izsvák S.F. De Meyer A. Athanassiadou D. Scherman
30. April 2018 / Genes Nutr ONS: an ontology for a standardized description of interventions and observational studies in nutrition F. Vitali R. Lombardo D. Rivero F. Mattivi P. Franceschi A. Bordoni A. Trimigno F. Capozzi G. Felici F. Taglino F. Miglietta N. De Cock C. Lachat B. De Baets G. De Tré M. Pinart K. Nimptsch T. Pischon J. Bouwman D. Cavalieri
28. Juni 2018 / Cell Physiol Biochem Pathway analysis hints towards beneficial effects of long-term vibration on human chondrocytes R. Lützenberg K. Solano C. Buken J. Sahana S. Riwaldt S. Kopp M. Krüger H. Schulz K. Saar N. Huebner R. Hemmersbach J. Bauer M. Infanger D. Grimm M. Wehland
17. Januar 2018 / Sci Rep The role of NFκB in spheroid formation of human breast cancer cells cultured on the Random Positioning Machine S. Kopp J. Sahana T. Islam A.G. Petersen J. Bauer T.J. Corydon H. Schulz K. Saar N. Huebner L. Slumstrup S. Riwaldt M. Wehland M. Infanger R. Luetzenberg D. Grimm
01. Juli 2018 / Genome Editing in Stem Cells and Regenerative Biology Genome engineering using Sleeping Beauty transposition in vertebrates S.S. Chilkunda V. Raghunathan S.A. Narayanavari Z. Ivics Z. Izsvák