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Blood Adv
Single-dose MGTA-145/plerixafor leads to efficient mobilization and in vivo transduction of HSCs with thalassemia correction in mice
- C. Li
- K.A. Goncalves
- T. Raskó
- A. Pande
- S. Gil
- Z. Liu
- Z. Izsvák
- T. Papayannopoulou
- J.C. Davis
- H.P. Kiem
- A. Lieber